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Showing articles 0 to 5 of 5 Filter Applied: gene therapy (Click to remove) X Linked Adrenoleukodystrophy:Clinical Presentation, Diagnosis, and Therapy JNNP 63:4-14, vanGeel,B.M.,et al, 1997 AAV9-Mediated Gene Therapy for Infantile-Onset Pompes Disease NEJM 392:2438-2446, 2477, Ma,X.,et al, 2025 Lentiviral Gene Therapy for Cerebral adrenoleukodystrophy NEJM 391:1302-1312,1358, Eichler,F.,et al, 2024 Muscular Dystrophies Lancet 394:2025-2038, Mercuri, E.,et al, 2019 Glycogen-Storage Disease Type II eMedicine, May 2, Ibrahim,J. &McGovern,M., 2006 Showing articles 0 to 5 of 5