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Current and Emerging Issues in Wilsons Disease
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Muscular Dystrophies
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Spinal Muscular Atrophy A Timely Review
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Diagnosis and Therapy in Neuromuscular Disorders: Diagnosis and New Treatments in Mitochondrial Diseases
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Gene Therapy for Duchenne Muscular Dystrophy: Expectations and Challenges
Arch Neurol 64:1236-1241, Rodino-Klapac,L.R.,et al, 2007
Glycogen-Storage Disease Type II
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Gene Transfer for Neurologic Disease
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Neurovirological Methods and Their Applications
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Neurogene Therapy for the 21st Century
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Gene Therapy for Cerebral Vascular Disease
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