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Showing articles 0 to 2 of 2 Filter Applied: progressive neurologic disorder (Click to remove) Niemann-Pick Type C Disease www.UpToDate.com, Nov, Schiffmann, R., 2026 Intrathecal 2-hydroxypropyl-�-cyclodextrin Decreases Neurological Disease Progression in Niemann-Pick disease, type C1: a non-randomised, open-label, phase 1-2 trial Lancet 390:1758-1768, Ory, D.S.,et al, 2017 Showing articles 0 to 2 of 2