A 23-Year-Old Woman Presenting with Cognitive Impairment and Gait Disturbance
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Leukodystrophies: Classification, Diagnosis, and Treatment
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Insights Into the Diagnosis and Treatment of Lysosomal Storage Diseases
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Long-Term Effects of Antidarsagene Autotemcel for Metachromatic Leukodystrophy
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Late Juvenile Metachromatic Leukodystrophy Treated with Bone Marrow Transplantation:A 4-Year Follow-up Study
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Longitudinal Neurophysiologic Studies in Pt with Metachromatic Leukodystrophy Following Bone Marrow Trnspl
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Organic Disease Presenting as a Psychiatric Syndrome
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