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Showing articles 0 to 2 of 2 Filter Applied: lysosomal storage disease (Click to remove) AAV9-Mediated Gene Therapy for Infantile-Onset Pompes Disease NEJM 392:2438-2446, 2477, Ma,X.,et al, 2025 Recurrent Acroparaesthesia During Febrile Infections Lancet 363:1698, Bodamer,O.A.,et al, 2004 Showing articles 0 to 2 of 2